Gene Therapy Pipeline
How does it work
What is Gene Therapy
Human gene therapy seeks to modify or manipulate the expression of a gene or to alter the biological properties of living cells for therapeutic use. Gene therapy is a technique that modifies a person’s genes to treat or cure disease. Gene therapies can work by several mechanisms: Replacing a disease-causing gene with a healthy copy of the gene, inactivating a disease-causing gene that is not functioning properly, and introducing a new or modified gene into the body to help treat disease. Gene therapy products are being studied to treat diseases including cancer, genetic diseases (like hearing loss and deafness), and infectious diseases.
Gene Therapy products are becoming medically and commercially viable.
Status Of RHI Product Line
Developing Therapeutic Solutions for Hearing Loss
Targets individuals born with progressive hearing loss.
Targets major cause of non-syndromic hearing loss. POC studies underway.
Targets hearing loss prevalent in the Cochlear Implant population. POC studies underway.